Rare Disease Day 2024

Rare Disease Day 2024 share your colors banner. Diverse group of people proudly standing in front of RDD logo.

Orphan Products for Rare Diseases: Availability and Accessibility - They're Not The Same Thing

Thursday, March 7, 2024 | McNamara Alumni Center and online

RSVP

Keynote speakers:

David Fajgenbaum

David Fajgenbaum, MD, MBA, MSc

Associate Professor of Medicine
Director, Center for Cytokine Storm Treatment & Laboratory
Associate Director, Patient Impact, Orphan Disease Center
University of Pennsylvania
Co-Founder & President, Castleman Disease Collaborative Network
Co-Founder & President, Every Cure

 

“From Chasing My Cure to Every Cure: Leveraging AI to unlock the full potential of every medicine.”

 
 
David McLean

David J. McLean, PhD

Chief Executive Officer of Emerging Therapy Solutions

“The Multiple Challenges in Accessing Orphan Products for Patients, Families and Clinicians”

Schedule of events

9:00–10:00 am | Patient Advocacy Group Breakfast
*presentation by Susan Berry, MD about the UMN Rare Disease Center of Excellence*
10:30–12:00 pm | Poster Symposium
12:00–2:00 pm | Formal Program

Poster Symposium

The poster symposium is an opportunity for event attendees to share their research on basic, translational, and clinical research related to rare diseases and their treatments. Posters do not have to be new - you can re-purpose one that has already been presented somewhere else. The poster symposium will open at 10:30 am.

Research Awards

To be considered for a research award, trainees must submit a personal statement with their abstract submission on how their research or research path contributes to the understanding and/or treatment of rare diseases. Three posters will be selected to receive this award. The author of each personal statement will receive a gift card.