Thursdays from 11:15am-12:30pm
MTRF 3–204 or Zoom
| Date | Title |
|---|---|
September 10 | The Del-zota Clinical Development Journey in DMD44 | Alan Roloff, PhD, Principal Medical Science Liaison; Avidity Biosciences |
| September 17 | The Clinical Development of Zorevunersen, an Investigational Antisense Oligonucleotide for Dravet Syndrome | Bethany Bedford, PharmD, Regional Medical Director, Stoke Therapeutics, Inc. |
| September 24 | Sharing Summary-Level Study Results with Clinical Research Participants | Adeboye Bamgboye, BPharm, ECP PhD candidate |
| October 1 | FDA and the Regulations Governing Clinical Trials: An Overview | Marie Kuker, RPh, FRAPS, RAC, President, Kuker Regulatory Consulting LLC |
| October 8 | Submitting an IND: What We Need to Know | Nathan Phan, ECP Graduate student, CODR |
| October 15 | Clinical Evidence and Long-Term Outcomes in Dravet Syndrome and Lennox-Gastaut Syndrome | Heidi Henniger, MD, FAAN, FAES, Clinical Advisor, UCB Inc. |
| October 22 | A Comprehensive Review of Azetukalner for Focal Seizures-MOA and Clinical Trial Results | Michele Faulkner, PharmD, FASHP, Sr. Medical Science Liaison, Xenon Pharmaceuticals |
| October 29 | Advancing Acromegaly care with Paltusotine (Palsonify®) | Beth Babler, PhD, APNP, CDCES, Sr. Medical Science Liaison, Crinetics Pharmaceuticals |
| November 5 | IND Maintenance: How to take care of your IND | Mohamed S. Fayed, BPharm, MS, PhD candidate, CODR |
| November 12 | An Endpoint-enabling Natural History Study for Dup15q Syndrome | Dylan Ritter, PhD, Director, Scientific and Clinical Initiatives, Dup15q alliance |
| November 19 | Gene Therapy in Lysosomal Diseases | Jeffrey Gaynes, MS, ECP Graduate student, CODR |
| November 26 | No Seminar | Thanksgiving Holiday |
| December 3 | Understanding the Gut Microbiome in Gaucher Disease | Raghu Rai Sharma, MPharm, PhD, Postdoctoral Associate, CODR |
| December 10 | Rare Disease Management – Trends from 2024 Approvals | David M. Stefanoni, MS, VP Pharma Strategy & Relations, Fairview Pharmacy Solutions |