Rare Disease Day 2021

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February 26, 2021 Rare Disease Day Presentation

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Introducton From Joan T.A. Gabel

Patient Advocacy Groups

The ALS Association
Autoimmune Hepatitis Association
EBlifestyle*
Engage Health*
Epilepsy Foundation of Minnesota*
Ethan's Reason
Hemophilia Foundation of MN/Dakotas*
IndoUSrare*
Kidz1stFund
Lennox-Gastaut Syndrome (LGS) Foundation*
Minnesota Council on Disability*
Minnesota Rare Action Network
National Ataxia Foundation*
National Marrow Donor Program/ Be The Match
Organic Acidemia Association*
Rein in Sarcoma*
Research to the People*
Retina South Africa
Sickle Cell Foundation of Minnesota
United Mitochondrial Disease Foundation*
Usher Syndrome Coalition*
Yaya Foundation for 4h Leukodystrophy


*hosted exhibit table

Rare Disease Day Proclamation

Sponsors

Bluebird Bio
Bristol Myers Squibb
Fairview Pharmacy Services
Greenwich Biosciences
Horizon Therapeutics
Jeeva Informatics Solutions
Ligand Pharmaceuticals
Novartis
Nucleus Network
Orchard Therapeutics
Takeda Pharmaceuticals
Zogenix