Rare Disease Day 2018
Gene Therapy for Rare Diseases: Promise and Challenges
Thank you to all who joined us!
First year College of Pharmacy students and Dr. Jim Cloyd
Keynote: Drs. Beau Webber, Michelle Berg, Mark Osborn
Patient Advocacy Group
Q-A moderator, Dr Jakub Tolar
Q-A moderator, Dr Jakub Tolar
Rare Disease Day Research Awardees
Viewing Posters
Erica Barnes co-founder Chloe's Fight Rare Disease Foundation
Keynote Speakers
Beau Webber, PhD
Advancing Next Generation Gene & Cell Therapies for Epidermolysis Bullosa
Assistant Professor, Pediatric Hematology and Oncology, University of Minnesota
View Presentation
Mark Osborn, PhD
Hematopoietic Lineage Cell Engineering for Rare Diseases
Assistant Professor, Department of Pediatrics, University of Minnesota
View Presentation
Michelle Berg
Passion, Perspective, and Progress: One Community’s Ongoing Drive to Develop a Potential Gene Therapy for a Rare Pediatric Disease
Vice President, Patient Affairs and Community Engagement, Abeona Therapeutics
View Presentation
Program and Poster Abstracts
Moderator
Jakub Tolar, MD, PhD
Dean, Medical School, University of Minnesota
Closing Remarks
James Cloyd III, PharmD
Professor, Department of Experimental and Clinical Pharmacology (ECP), University of Minnesota
Co-Sponsors
Center for Orphan Drug Research, University of Minnesota & Stem Cell Institute, University of Minnesota