Rare Disease Day 2018

Gene Therapy for Rare Diseases: Promise and Challenges

Thank you to all who joined us!

First year College of Pharmacy students and Dr Jim Cloyd

First year College of Pharmacy students and Dr. Jim Cloyd

Keynote Speakers; Dr. Beau Webber, Dr. Michelle Berg, Dr. Mark Osborn

Keynote: Drs. Beau Webber, Michelle Berg, Mark Osborn

Patient Advocacy Group

Patient Advocacy Group

Q_A moderator, Dr Jakub Tolar

Q-A moderator, Dr Jakub Tolar

Q_A moderator, Dr Jakub Tolar

Q-A moderator, Dr Jakub Tolar

Rare Disease Day Research Awardees

Rare Disease Day Research Awardees

Viewing posters

Viewing Posters

Welcome, Erica Barnes co-founder Chloe_s Fight Rare Disease Foundation

Erica Barnes co-founder Chloe's Fight Rare Disease Foundation

      

Keynote Speakers

Beau WebberBeau Webber, PhD
Advancing Next Generation Gene & Cell Therapies for Epidermolysis Bullosa

Assistant Professor, Pediatric Hematology and Oncology, University of Minnesota
View Presentation

Mark Osborn

 

Mark Osborn, PhD
Hematopoietic Lineage Cell Engineering for Rare Diseases

Assistant Professor, Department of Pediatrics, University of Minnesota
View Presentation

Michelle Berg

Michelle Berg
Passion, Perspective, and Progress: One Community’s Ongoing Drive to Develop a Potential Gene Therapy for a Rare Pediatric Disease

Vice President, Patient Affairs and Community Engagement, Abeona Therapeutics
View Presentation

Rare Disease Day 2018

Program and Poster Abstracts

Moderator

Jakub TolarJakub Tolar, MD, PhD
Dean, Medical School, University of Minnesota



Closing Remarks

James CloydJames Cloyd III, PharmD
Professor, Department of Experimental and Clinical Pharmacology (ECP), University of Minnesota

Co-Sponsors

Center for Orphan Drug Research, University of Minnesota & Stem Cell Institute, University of Minnesota