Rare Disease Day - Clinical Gene Therapy: The Future is Now


Clinical Gene Therapy: The Future is Now

This year's program will further our understanding of gene therapy by hearing from a clinician and a panel of patients and parents. The clinician will provide an overview of current therapies and therapies that are in the pipeline, whereas the panel will feature patients who are currently receiving gene therapy and parents of children who are potential recipients.  All are welcome to this free event. 

RSVP and Abstract Submission

Research Poster Abstract Submission

Research poster abstract submissions will be accepted on basic, translational, and clinical research related to rare diseases and their treatments. 

Co-Sponsors of Rare Disease Day

Center of Orphan Drug Researh & Stem Cell Institute


keynoteJames M. Wilson, MD, PhD

Rose H. Weiss Professor and Director
Orphan Disease Center, University of Pennsylvania


Patient Perspectives on Gene Therapy - Patients and caregivers representing several rare disease communities share their thoughts, hopes and concerns regarding gene therapy

rdd logo


Friday, March 1st, 2019
11:00am to 2:30pm


Graduate Hotel, Minneapolis, MN


Patient Advocacy Group Breakfast

Poster Session
Research posters related to rare diseases or orphan drug research from investigators and their trainees





Joint Accreditation LogoIn support of improving patient care, University of Minnesota, Interprofessional Continuing Education is jointly accredited by the Accreditation Council for Continuing Medical Education (ACCME), the Accreditation Council for Pharmacy Education (ACPE), and the American Nurses Credentialing Center (ANCC) to provide continuing education for the healthcare team.


Credit Designation Statements

American Medical Association (AMA)

This activity has been approved for AMA PRA Category 1 Credit™. Determination of exact number of credits is pending.

Accreditation Council for Pharmacy Education (ACPE)

This activity is eligible for ACPE credit; see final CPE activity announcement for specific details.

Other Healthcare Professionals

Other healthcare professionals who participate in this CE activity may submit their statement of participation to their appropriate accrediting organizations or state boards for consideration of credit. The participant is responsible for determining whether this activity meets the requirements for acceptable continuing education.