Therapies for the Few, Impact for Many: Rethinking How We Develop Rare Disease Treatments
Thursday, March 5, 2026
Attend in-person or virtually
McNamara Alumni Center (200 Oak St SE, Minneapolis MN)
2026 Speakers
Robert Schuck, PharmD, PhD Deputy Director, Division of Translational and Precision MedicineOffice of Clinical PharmacologyCDER, FDA
"Advancing Orphan Drug Development Through Regulatory Innovation"
Margot Cousin, PhD, Assistant Professor of Medical Genetics, Department of Molecular Medicine, Department of Neurology, Director N-of-1 Therapeutics Program, Center for Individualized Medicine, Mayo Clinic
"From small n to Big N: Learning, Scaling, and Transforming Rare Disease Care"
Sharon King, Chief Operating Officer National MPS Society
"When Purpose Aligns: Patients, Science, and Shared Resolve"
Patient Advocacy Breakfast 2026
"Navigating Healthcare Delivery in an Evolving Legislative Landscape: PAG Perspectives on Case Management and Medicaid Services"
Moderated by Erica Barnes, Executive Director, Minnesota Rare Disease Advisory Council